New Berlin Mother Pleads for FDA Approval of a New Drug to Save Her Son From Terminal Hunter Syndrome

New Berlin mother pleads for FDA approval of a new drug to save her son from terminal Hunter Syndrome

A New Berlin mother is waiting for the FDA to approve a new drug that could save her son from a fatal genetic disorder.Rory Jaskulski is a kindergarten student at Orchard Lane School. He is known for his bright smile and energy.Orchard Lane School Principal Royce Linder sees Rory Jaskulski's joy every day."Really, when it comes down to it, hes just a kindergarten student. He wants the same thing out of kindergarten that every kindergartener want…

Denali Therapeutics CEO: 2026 Pivotal With Hunter Syndrome FDA Decision and New TV Trial Readouts

Denali Therapeutics (NASDAQ:DNLI) founder and CEO Ryan Watts said 2026 is shaping up to be a pivotal year for the company as it approaches a potential first product approval and advances multiple transport vehicle-enabled programs across rare disease and neurodegeneration. Speaking in a moderated discussion, Watts highlighted the company’s pending FDA decision for tividenofusp alfa […]